CE for Pharmacists & Technicians: Gene Therapies in Sickle Cell Disease: Review Article
by Anthony E. Rende, 2026 PharmD Candidate, Kevin A. Look, PharmD, PhD
Abstract:
This article reviews sickle cell disease treatments with an emphasis on newly approved gene therapies. It examines the patient journey to achieving a potential cure with gene therapy while addressing its barriers. Additionally, it explores pharmacoeconomic considerations and the payer landscape, both of which play a large role in patients’ access to these groundbreaking therapies.
Learning Objectives
Download PDF
2025 May/June Table of Contents
Abstract:
This article reviews sickle cell disease treatments with an emphasis on newly approved gene therapies. It examines the patient journey to achieving a potential cure with gene therapy while addressing its barriers. Additionally, it explores pharmacoeconomic considerations and the payer landscape, both of which play a large role in patients’ access to these groundbreaking therapies.
Learning Objectives
- Identify the current available treatment options for sickle cell disease and their limitations
- Describe the patient journey for receiving gene therapy for sickle cell disease
- Explain pharmacoeconomic and payer landscape challenges affecting access to gene therapies for sickle cell disease
Download PDF
2025 May/June Table of Contents